Oral Presentation 22nd Annual Lorne Proteomics Symposium 2017

Coupling of gene-editing and proteomics to dissect the assembly and function of human mitochondrial complex I (#45)

David A Stroud 1 , Elliot E Surgenor 1 , Luke E Formosa 1 2 , Boris Reljic 2 , Ann E Frazier 3 4 , Marris G Dibley 1 , Laura D Osellame 1 , Tegan Stait 3 , Traude H Beilharz 1 , David R Thorburn 3 4 , Agus Salim 5 , Michael T Ryan 1
  1. Department of Biochemistry and Molecular Biology, Monash Biomedicine Discovery Institute, Monash University, Melbourne, Victoria, Australia
  2. Department of Biochemistry and Genetics, La Trobe Institute for Molecular Science, Melbourne, Victoria, Australia
  3. Murdoch Childrens Research Institute, Royal Children’s Hospital, Melbourne, Victoria, Australia
  4. Department of Pediatrics, University of Melbourne, Melbourne, Victoria, Australia
  5. Department of Mathematics and Statistics, La Trobe University, Melbourne, Victoria, Australia

Complex I (NADH:ubiquinone oxidoreductase) is the first enzyme of the mitochondrial respiratory chain and is composed of 45 subunits in humans, making it one of the largest known multi-subunit membrane protein complexes. Complex I exists in supercomplex forms with respiratory chain complexes III and IV, which are together required for the generation of a transmembrane proton gradient used for the synthesis of ATP. Complex I is also a major source of damaging reactive oxygen species and its dysfunction is associated with mitochondrial disease, Parkinson’s disease and ageing. Bacterial and human complex I share 14 core subunits that are essential for enzymatic function; however, the roles and necessity of the remaining 31 human accessory subunits is unclear. The incorporation of accessory subunits into the complex increases the cellular energetic cost and has necessitated the involvement of numerous assembly factors for complex I biogenesis.

We used gene-editing technology to generate human knockout cell lines for each accessory subunit. We show that 25 subunits are strictly required for assembly of a functional complex, and one subunit is essential for cell viability. Comprehensive quantitative proteomic analysis of all cell lines revealed that loss of each subunit affects the stability of other subunits residing in the same structural module. Analysis of proteomic changes after the loss of specific modules revealed two new assembly factors required for building the distal portion of the complex I membrane arm. Our results demonstrate the broad importance of accessory subunits in the structure and function of human complex I.

Coupling gene-editing technology with large scale proteomics represents a powerful tool for dissecting multisubunit complexes and enabling the study of complex dysfunction at a cellular level.